Research to develop new rare disease therapies underway at The Jackson Laboratory
NIH grant will support new gene editing-based therapeutic approaches for four neurological conditions By Mark Wanner BAR HARBOR, Maine, June 6, 2023 /PRNewswire/ — Researchers led by Cathleen Lutz, Ph.D., are using an exciting new method, preclinical genomic editing, to develop safe, effective therapies for rare diseases and bring them to the clinic. Unfortunately, the translation … Read more