PPMD Applauds FDA for Landmark Approval of First-Ever Gene Therapy Treatment for Duchenne for Patients Ages 4-5 Years Old
Organization Will Continue to Support Patient Access and Drive Policies and Projects That Support Development and Approval of More Therapies WASHINGTON, June 22, 2023 /PRNewswire/ — Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), heralded today’s decision by the Food and Drug Administration (FDA) to approve … Read more